About:

The World Orphan Drug Congress USA is the leading global event for the rare disease and orphan drug ecosystem. Held at the Thomas M. Menino Convention & Exhibition Center in Boston, the 2026 edition is expected to convene more than 2,000 attendees from over 50 countries across three days of pre-congress workshops, plenary sessions, and partnering meetings.

The program brings together pharmaceutical and biotechnology executives, government regulators, patient advocates, payers, investors, and solution providers, with thematic streams covering patient data, next-generation therapies, clinical development and regulation, pricing and reimbursement, AI and digital health, diagnosis and drug discovery, early access programs, and real-world evidence. With the Inflation Reduction Act actively reshaping the orphan drug landscape, the 2026 program centers on regulatory and market-access strategy at a pivotal moment for the field.

For leaders in rare disease — across R&D, commercial, regulatory, and investment — this is the year's defining convergence point.

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